Orphan designation: Humanised anti-folate receptor 1 monoclonal antibody conjugated to maytansinoid DM4 Treatment of ovarian cancer, 19/03/2015 Positive

Orphan designation: Humanised anti-folate receptor 1 monoclonal antibody conjugated to maytansinoid DM4 Treatment of ovarian cancer, 19/03/2015 Positive

Orphan designation: Heterologous human adult liver-derived progenitor cells Treatment of ornithine-translocase deficiency, 17/07/2013 Positive

Orphan designation: Heterologous human adult liver-derived progenitor cells Treatment of ornithine-translocase deficiency, 17/07/2013 Positive

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