Metamizole-containing medicinal products article 107i referral - Timetable for the procedure
Orphan designation: nizubaglustat Treatment of GM1 gangliosidosis, 28/06/2024 Positive
Orphan designation: afatinib Treatment of complex regional pain syndrome, 28/06/2024 Positive
Orphan designation: Topiramate Treatment of neonatal encephalopathy, 28/06/2024 Positive
Orphan designation: Complement factor H Treatment of C3 glomerulopathy, 28/06/2024 Positive
Orphan designation: L-methionine Treatment of pulmonary alveolar proteinosis, 28/06/2024 Positive
Orphan designation: sargramostim Treatment of pulmonary alveolar proteinosis, 28/06/2024 Positive
Orphan designation: (R)-3-(1-Cyclopropyl-3-(2-fluoro-4-(trifluoromethoxy)benzyl)ureido)piperidine-1-carboxamide Treatment of hyperphenylalaninaemia, 28/06/2024 Positive
Orphan designation: apilimod Treatment of amyotrophic lateral sclerosis, 28/06/2024 Positive
Orphan designation: Ethyl(2E,4S)-4-({(2S)-2-[3-{[(5-methyl-1,2-oxazol-3-yl)carbonyl]amino}-2-oxopyridin-1(2H)-yl]pent-4-ynoyl}amino)-5-[(3S)-2-oxopyrrolidin-3-yl]pent-2-enoate, Pocapavir Treatment of poliovirus infection, 28/06/2024 Positive