Submitted by Anonymous (not verified) on 13 September 2023 - 14:57
Orphan designation: 2-[6-(6,7-Dimethoxyquinolin-3-yl)pyridin-3-yl]-N-[3-(1,1,1-trifluoro-2-methylpropan-2-yl)-1,2-oxazol-5-yl]acetamide (zeteletinib), Treatment of medullary thyroid carcinoma, 19/02/2021, Positive
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