Orphan designation: Fosmanogepix Treatment of fusariosis, 15/02/2023 Positive
Submitted by Anonymous (not verified) on 15 October 2024 - 10:33
Orphan designation: Fosmanogepix Treatment of fusariosis, 15/02/2023 Positive
Orphan designation: Heterologous human adult liver derived stem cells Treatment of ornithinine transcarbamylase deficiency, 04/02/2008 Positive
Submitted by Anonymous (not verified) on 15 October 2024 - 10:09
Orphan designation: Heterologous human adult liver derived stem cells Treatment of ornithinine transcarbamylase deficiency, 04/02/2008 Positive
Orphan designation: Heterologous human adult liver-derived progenitor cells Treatment of citrullinaemia type 1, 17/07/2013 Positive
Submitted by Anonymous (not verified) on 15 October 2024 - 9:40
Orphan designation: Heterologous human adult liver-derived progenitor cells Treatment of citrullinaemia type 1, 17/07/2013 Positive
Orphan designation: Heterologous human adult liver-derived stem cells Treatment of Crigler-Najjar syndrome, 29/11/2007 Positive
Submitted by Anonymous (not verified) on 15 October 2024 - 8:00
Orphan designation: Heterologous human adult liver-derived stem cells Treatment of Crigler-Najjar syndrome, 29/11/2007 Positive
Orphan designation: Heterologous human adult liver-derived progenitor cells Treatment of hyperargininaemia, 17/07/2013 Positive
Submitted by Anonymous (not verified) on 15 October 2024 - 8:00
Orphan designation: Heterologous human adult liver-derived progenitor cells Treatment of hyperargininaemia, 17/07/2013 Positive
Orphan designation: Heterologous human adult liver-derived progenitor cells Treatment of carbamoyl-phosphate synthase-1 deficiency, 17/07/2013 Positive
Submitted by Anonymous (not verified) on 15 October 2024 - 8:00
Orphan designation: Heterologous human adult liver-derived progenitor cells Treatment of carbamoyl-phosphate synthase-1 deficiency, 17/07/2013 Positive
Orphan designation: Heterologous human adult liver-derived progenitor cells Treatment of citrullinaemia type 2, 17/08/2013 Positive
Submitted by Anonymous (not verified) on 15 October 2024 - 7:50
Orphan designation: Heterologous human adult liver-derived progenitor cells Treatment of citrullinaemia type 2, 17/08/2013 Positive
Orphan designation: Heterologous human adult liver-derived progenitor cells Treatment of N-acetylglutamate synthetase (NAGS) deficiency, 17/07/2013 Positive
Submitted by Anonymous (not verified) on 15 October 2024 - 7:50
Orphan designation: Heterologous human adult liver-derived progenitor cells Treatment of N-acetylglutamate synthetase (NAGS) deficiency, 17/07/2013 Positive
Human medicines European public assessment report (EPAR): Siklos, hydroxycarbamide, Date of authorisation: 29/06/2007, Revision: 26, Status: Authorised
Submitted by Anonymous (not verified) on 14 October 2024 - 14:21
Human medicines European public assessment report (EPAR): Siklos, hydroxycarbamide, Date of authorisation: 29/06/2007, Revision: 26, Status: Authorised
Veterinary medicines European public assessment report (EPAR): Versican Plus Pi/L4R, canine parainfluenza virus, leptospira and rabies virus, Status: Authorised
Submitted by Anonymous (not verified) on 14 October 2024 - 14:01
Veterinary medicines European public assessment report (EPAR): Versican Plus Pi/L4R, canine parainfluenza virus, leptospira and rabies virus, Status: Authorised