Submitted by Anonymous (not verified) on 15 October 2024 - 7:50
Orphan designation: Heterologous human adult liver-derived progenitor cells Treatment of N-acetylglutamate synthetase (NAGS) deficiency, 17/07/2013 Positive
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Orphan designation: Heterologous human adult liver-derived progenitor cells Treatment of N-acetylglutamate synthetase (NAGS) deficiency, 17/07/2013 Positive