EMEA-003215-PIP01-22-M01
Submitted by Anonymous (not verified) on 5 June 2025 - 15:38
EMEA-003215-PIP01-22-M01
NovoSeven (eptacog alfa)
Submitted by Anonymous (not verified) on 5 June 2025 - 15:25
NovoSeven (eptacog alfa)
PSUSA/00000795/202410
Submitted by Anonymous (not verified) on 5 June 2025 - 15:05
PSUSA/00000795/202410
Highlights - Second EMA / Alliance for Regenerative Medicine bilateral meeting
Submitted by Anonymous (not verified) on 5 June 2025 - 14:48
Highlights - Second EMA / Alliance for Regenerative Medicine bilateral meeting
Orphan designation: defibrotide Prevention of hepatic veno-occlusive disease, 29/07/2004 Withdrawn
Submitted by Anonymous (not verified) on 5 June 2025 - 14:45
Orphan designation: defibrotide Prevention of hepatic veno-occlusive disease, 29/07/2004 Withdrawn
Orphan designation: defibrotide Prevention of graft-versus-host disease, 13/11/2013 Withdrawn
Submitted by Anonymous (not verified) on 5 June 2025 - 14:40
Orphan designation: defibrotide Prevention of graft-versus-host disease, 13/11/2013 Withdrawn
Orphan designation: Ganaxolone Treatment of CDKL5 deficiency disorder, 13/11/2019 Positive
Submitted by Anonymous (not verified) on 5 June 2025 - 14:34
Orphan designation: Ganaxolone Treatment of CDKL5 deficiency disorder, 13/11/2019 Positive
Orphan designation: single guide RNA targeting the human TTR gene, Ziclumeran Treatment of ATTR amyloidosis, 26/03/2021 Positive
Submitted by Anonymous (not verified) on 5 June 2025 - 14:28
Orphan designation: single guide RNA targeting the human TTR gene, Ziclumeran Treatment of ATTR amyloidosis, 26/03/2021 Positive
Orphan designation: Copper (64Cu) oxodotreotide Diagnosis of neuroendocrine neoplasms, 09/12/2022 Positive
Submitted by Anonymous (not verified) on 5 June 2025 - 14:26
Orphan designation: Copper (64Cu) oxodotreotide Diagnosis of neuroendocrine neoplasms, 09/12/2022 Positive
Orphan designation: Ganaxolone Treatment of tuberous sclerosis, 15/10/2021 Positive
Submitted by Anonymous (not verified) on 5 June 2025 - 14:25
Orphan designation: Ganaxolone Treatment of tuberous sclerosis, 15/10/2021 Positive