Orphan designation: octreotide hydrochloride Treatment of autosomal dominant polycystic kidney disease, 18/07/2025 Positive
Orphan designation: phosphorodiamidate morpholino oligonucleotide against the CUG repeat expansion of the DMPK gene mRNA transcript, conjugated to a cell penetrating peptide Treatment of dystrophic myotonia, 18/07/2025 Positive
Orphan designation: resecabtagene autoleucel Treatment of idiopathic inflammatory myopathy, 18/07/2025 Positive
Orphan designation: Elafibranor Treatment of primary sclerosing cholangitis, 18/07/2025 Positive
Orphan designation: nuvisertib Treatment of myelofibrosis, 18/07/2025 Positive
Rules for reimbursement of expenses for delegates attending meetings with effect from 17 March 2023
Veterinary medicines European public assessment report (EPAR): Clevor, ropinirole, Status: Authorised
Veterinary medicines European public assessment report (EPAR): Chanhold, selamectin, Status: Authorised
PSUSA/00002153/202412
Veterinary medicines European public assessment report (EPAR): Baycox Iron, toltrazuril,iron (III) ion, Status: Authorised