Submitted by Anonymous (not verified) on 19 September 2023 - 16:00
Human medicines European public assessment report (EPAR): Strimvelis, autologous CD34+ enriched cell fraction that contains CD34+ cells transduced with retroviral vector that encodes for the human ADA cDNA sequence, Severe Combined Immunodeficiency, Date of authorisation: 26/05/2016, Revision: 9, Status: Authorised
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