Orphan designation: adenovirus associated viral vector serotype 5 containing the human pde6β gene Treatment of retinitis pigmentosa, 19/06/2013 Positive
Meeting highlights from the Committee for Veterinary Medicinal Products (CVMP) 8-10 October 2024
Summary of opinion: Eluracat Positive
Orphan designation: Allogeneic umbilical cord-derived mesenchymal stromal cells, pooled Treatment of perinatal asphyxia, 13/12/2023 Positive
Orphan designation: Humanised IgG1 kappa antibody against serum amyloid A and AL amyloid Treatment of amyloid light-chain amyloidosis, 08/02/2013 Positive
Human medicines European public assessment report (EPAR): Xadago, safinamide, Date of authorisation: 23/02/2015, Revision: 15, Status: Authorised
Orphan designation: Treatment of progressive familial intrahepatic cholestasis, 17/07/2012 Positive
Orphan designation: 2S, 4R ketoconazole Treatment of Cushing's syndrome, 04/07/2012 Positive
Orphan designation: Flucytosine Treatment of glioma, 22/02/2018 Positive
Orphan designation: Vocimagene amiretrorepvec Treatment of glioma, 22/02/2018 Positive