Orphan designation: Humanised IgG4 monoclonal antibody against active complement component 1, subcomponent s Treatment of chronic inflammatory demyelinating polyneuropathy, 22/05/2023 Positive

Orphan designation: Humanised IgG4 monoclonal antibody against active complement component 1, subcomponent s Treatment of chronic inflammatory demyelinating polyneuropathy, 22/05/2023 Positive

Orphan designation: Adeno-associated virus serotype 9 expressing a transcription factor for the SCN1A gene Treatment of Dravet syndrome, 22/05/2023 Positive

Orphan designation: Adeno-associated virus serotype 9 expressing a transcription factor for the SCN1A gene Treatment of Dravet syndrome, 22/05/2023 Positive

Newsletters

Stay informed on our latest news!

CAPTCHA

This question is for testing whether or not you are a human visitor and to prevent automated spam submissions.