Submitted by Anonymous (not verified) on 24 January 2024 - 14:00
Orphan designation: Messenger RNA encoding Cas9, Single guide RNA targeting the human KLKB1 gene Treatment of hereditary angioedema, 11/08/2023 Positive
Source:
Orphan designation: Messenger RNA encoding Cas9, Single guide RNA targeting the human KLKB1 gene Treatment of hereditary angioedema, 11/08/2023 Positive