Submitted by Anonymous (not verified) on 24 January 2024 - 12:06
Orphan designation: Adeno-associated virus serotype 9 expressing a transcription factor for the SCN1A gene Treatment of Dravet syndrome, 22/05/2023 Positive
Source:
Orphan designation: Adeno-associated virus serotype 9 expressing a transcription factor for the SCN1A gene Treatment of Dravet syndrome, 22/05/2023 Positive