Submitted by Anonymous (not verified) on 25 January 2024 - 8:09
Orphan designation: patidistrogene bexoparvovec Treatment of limb girdle muscular dystrophy, 15/02/2023 Positive
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Orphan designation: patidistrogene bexoparvovec Treatment of limb girdle muscular dystrophy, 15/02/2023 Positive