Submitted by Anonymous (not verified) on 2 February 2024 - 14:39
Orphan designation: Humanised IgG1 kappa fragment antibody targeting TfR1 conjugated to P125 oligonucleotide Treatment of myotonic disorders, 22/05/2023 Positive
Source:
Orphan designation: Humanised IgG1 kappa fragment antibody targeting TfR1 conjugated to P125 oligonucleotide Treatment of myotonic disorders, 22/05/2023 Positive