Submitted by Anonymous (not verified) on 2 February 2024 - 9:40
Orphan designation: Virus-like particle containing Cas9/gRNA ribonucleoprotein targeting the human HTT gene Treatment of Huntington’s disease, 16/08/2023 Positive
Source:
Orphan designation: Virus-like particle containing Cas9/gRNA ribonucleoprotein targeting the human HTT gene Treatment of Huntington’s disease, 16/08/2023 Positive