Submitted by Anonymous (not verified) on 22 August 2024 - 15:38
Orphan designation: (R)-3-(1-Cyclopropyl-3-(2-fluoro-4-(trifluoromethoxy)benzyl)ureido)piperidine-1-carboxamide Treatment of hyperphenylalaninaemia, 28/06/2024 Positive
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