Submitted by Anonymous (not verified) on 22 August 2024 - 15:30
Orphan designation: (R)-(3-(2'-cyclopropyl-3-(hydroxymethyl)-[1,1'-biphenyl]-4-yl) pyrrolidin-1-yl)(5-fluoropyridin-2-yl)methanone Treatment of pachyonychia congenita, 28/06/2024 Positive
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