Submitted by Anonymous (not verified) on 21 November 2024 - 15:59
Orphan designation: 4-[[(4-Methoxyphenyl)thio]methyl]-N,N-dimethyl-1H-1,2,3-triazole-1-ethanamine Treatment of non-syndromic inherited retinal dystrophies with a rod-dominant phenotype, 11/11/2024 Positive
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