Orphan designation: Autologous bone marrow derived CD34+ cells transduced ex vivo with a self-inactivating lentiviral vector containing a normal version of the coding region of the IL2RG gene Treatment of X-linked severe combined immunodeficiency, 13/11/2

Orphan designation: Autologous bone marrow derived CD34+ cells transduced ex vivo with a self-inactivating lentiviral vector containing a normal version of the coding region of the IL2RG gene Treatment of X-linked severe combined immunodeficiency, 13/11/2020 Withdrawn