Submitted by Anonymous (not verified) on 5 June 2025 - 14:28
Orphan designation: single guide RNA targeting the human TTR gene, Ziclumeran Treatment of ATTR amyloidosis, 26/03/2021 Positive
Source:
Orphan designation: single guide RNA targeting the human TTR gene, Ziclumeran Treatment of ATTR amyloidosis, 26/03/2021 Positive