Submitted by Anonymous (not verified) on 5 June 2025 - 14:05
Orphan designation: posnafusp alfa Treatment of mucopolysaccharidosis type IIIA (Sanfilippo A syndrome), 14/01/2022 Positive
Source:
Orphan designation: posnafusp alfa Treatment of mucopolysaccharidosis type IIIA (Sanfilippo A syndrome), 14/01/2022 Positive