Submitted by Anonymous (not verified) on 30 June 2025 - 13:10
Orphan designation: Induced pluripotent stem cells-derived myogenic progenitor cells Treatment of Becker muscular dystrophy, 22/05/2025 Positive
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Orphan designation: Induced pluripotent stem cells-derived myogenic progenitor cells Treatment of Becker muscular dystrophy, 22/05/2025 Positive