Submitted by Anonymous (not verified) on 17 July 2025 - 14:02
Orphan designation: (2S,4R)-1-(2-(3-acetyl-5-(2-methylpyrimidine-5-yl)-1H-indazol-1-yl)acetyl)-N-(6-bromopyridine-2-yl)-4-fluoropyrrolidine-2-carboxamide Treatment of C3 glomerulopathy, 21/03/2018 Withdrawn
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