Submitted by Anonymous (not verified) on 25 July 2025 - 11:24
Orphan designation: 2-[[Hydroxy[(R)-2-[((5Z,8Z,11Z,14Z)-eicosa-5,8,11,14-tetraenoyl)oxy]-3-(octadecyloxy)propoxy]phosphoryl]oxy]ethan-1-amine Treatment of Rett syndrome, 20/06/2025 Positive
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