Submitted by Anonymous (not verified) on 10 April 2026 - 13:30
Orphan designation: (S)-1-(2,2-Difluoroethyl)-3-(difluoromethyl)-N-(1-(3-(2-methoxypyridin-4-yl)-1,2,4-oxadiazol-5-yl)ethyl)-1H-pyrazole-5-carboxamide Treatment of KCNT1-related epilepsy and neurodevelopmental disorders, 21/11/2025 Positive
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