Submitted by Anonymous (not verified) on 10 April 2026 - 10:49
Orphan designation: adeno-associated viral vector serotype ShH10 containing a codon-optimised human NDP gene Treatment of NDP gene-related disorders Positive
Source:
Orphan designation: adeno-associated viral vector serotype ShH10 containing a codon-optimised human NDP gene Treatment of NDP gene-related disorders Positive