Submitted by Anonymous (not verified) on 10 April 2026 - 10:38
Orphan designation: adeno-associated virus serotype 9 vector containing the human NDP gene Treatment of NDP gene-related disorders, 22/08/2025 Positive
Source:
Orphan designation: adeno-associated virus serotype 9 vector containing the human NDP gene Treatment of NDP gene-related disorders, 22/08/2025 Positive