Submitted by Anonymous (not verified) on 10 April 2026 - 10:23
Orphan designation: sonpiretigene isteparvovec Treatment of non-syndromic macular dystrophy, 22/08/2025 Positive
Source:
Orphan designation: sonpiretigene isteparvovec Treatment of non-syndromic macular dystrophy, 22/08/2025 Positive