Submitted by Anonymous (not verified) on 22 April 2026 - 15:47
Orphan designation: adeno-associated virus serotype SLB101 containing the human microdystrophin gene Treatment of Duchenne muscular dystrophy, 20/04/2026 Positive
Source:
Orphan designation: adeno-associated virus serotype SLB101 containing the human microdystrophin gene Treatment of Duchenne muscular dystrophy, 20/04/2026 Positive