Orphan designation: antisense oligonucleotide against SYNGAP1 regulatory RNA Treatment of SYNGAP1-related disorder, 20/04/2026 Positive | European Federation of Internal Medicine

Submitted by Anonymous (not verified) on 22 April 2026 - 15:43

Orphan designation: antisense oligonucleotide against SYNGAP1 regulatory RNA Treatment of SYNGAP1-related disorder, 20/04/2026 Positive

Link:

https://www.ema.europa.eu/en/medicines/human/orphan-designations/eu-3-26-3229

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