Submitted by Anonymous (not verified) on 18 May 2026 - 10:46
Orphan designation: 4-[(3S)-3-aminopyrrolidin-1-yl]-6-cyano-5-(3,5-difluorophenyl)-N-[(2S)-1,1,1-trifluoropropan-2-yl]pyridine-3-carboxamide Treatment of congenital hyperinsulinism, 09/12/2020 Withdrawn
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