Submitted by Anonymous (not verified) on 18 May 2026 - 9:53
Orphan designation: (S)-1-(4-(1-(3,4,5-trimethoxyphenyl)-1H-imidazol-4-ylamino)thieno[2,3-d]pyrimidin-2-yl)pyrrolidine-2-carboxamide Treatment of fibrodysplasia ossificans progressiva, 18/07/2022 Withdrawn
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