Orphan designation: 3-(Aminocarbonyl)-1-(2,3,5-tri-O-acetyl-beta-D-ribofuranosyl)-pyridinium chloride (1:1) Treatment of ataxia telangiectasia, 22/06/2026 Positive | European Federation of Internal Medicine

Submitted by Anonymous (not verified) on 24 August 2026 - 13:20

Orphan designation: 3-(Aminocarbonyl)-1-(2,3,5-tri-O-acetyl-beta-D-ribofuranosyl)-pyridinium chloride (1:1) Treatment of ataxia telangiectasia, 22/06/2026 Positive

Link:

https://www.ema.europa.eu/en/medicines/human/orphan-designations/eu-3-26-3254

Source:

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