Submitted by Anonymous (not verified) on 24 August 2026 - 10:34
Orphan designation: modified mRNA encoding human cystic fibrosis transmembrane conductance regulator Treatment of cystic fibrosis, 23/06/2026 Positive
Source:
Orphan designation: modified mRNA encoding human cystic fibrosis transmembrane conductance regulator Treatment of cystic fibrosis, 23/06/2026 Positive