Submitted by Anonymous (not verified) on 24 August 2026 - 10:21
Orphan designation: 1-({(5S,7S,8R)-8-Fluoro-3-[5-(2-hydroxypropan-2-yl)pyrazin-2-yl]-7-methyl-2-oxo-1-oxa-3-azaspiro[4.5]decan-7-yl}methyl)-1H-1,3-benzimidazole-6-carbonitrile Treatment of TRPV4-related neuromuscular disease, 28/07/2026 Positive
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